STAT+: Ultragenyx drug to treat Angelman syndrome, a rare disease, fails late-stage trial

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• STATCenter·1h ago

  STAT+: Ultragenyx drug to treat Angelman syndrome, a rare disease, fails late-stage trial

  Ultragenyx said its experimental therapy for Angelman syndrome, a rare disease, showed no benefit compared to a sham treatment in a Phase 3 trial.

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